With our increased understanding of the molecular mechanisms of haematological disorders, it has become possible to target therapy precisely to the underlying defect. Targeted therapy can increase safety and potency, while causing fewer side effects than standard treatment. "Smart" drugs and gene therapy have recently shown great promise in a wide range of malignant haematological and coagulation disorders.
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- 1 Haematology Department, Royal Perth Hospital, University of Western Australia, Perth, WA.
- 2 Haematology Department, Alfred Hospital, Melbourne, VIC.
- 3 Haematology Department, Mater Hospital, Brisbane, QLD.
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